New drug HMB-001 aims to curb dangerous bleeds in rare blood disorder

NCT ID NCT06211634

First seen Jan 02, 2026 · Last updated May 13, 2026 · Updated 27 times

Summary

This early-stage trial tests a new medicine called HMB-001 in about 57 people with Glanzmann thrombasthenia, a rare bleeding disorder. The study aims to see if the drug is safe and can reduce how often and how severely bleeds occur. Participants receive single or multiple doses over several months, with close monitoring for side effects and bleeding episodes.

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Contacts and locations

Locations

  • AP-HM - Hopital de la Timone

    Marseille, France

  • AP-HP Hopital Bicetre (Part B/C)

    Le Kremlin-Bicêtre, France

  • AP-HP Hopital Necker-Enfants Malades (Part B/C)

    Paris, France

  • Azienda Ospedaliero-Universitaria Careggi (Part B/C)

    Florence, Italy

  • Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano (Part B/C)

    Milan, Italy

  • Hemophilia Center of Western Pennsylvania (HCWP) (Part B/C)

    Pittsburgh, Pennsylvania, 15213, United States

  • Leeds Teaching Hospitals NHS Trust

    Leeds, United Kingdom

  • Mayo Clinic - Rochester (Part B/C)

    Rochester, Minnesota, 55905, United States

  • Queen Elizabeth Hospital Birmingham (Part B/C)

    Birmingham, United Kingdom

  • Richmond Pharmacology Ltd (Part A/B/C)

    London, United Kingdom

  • Royal Free London NHS Foundation Trust (Part B/C)

    London, United Kingdom

  • The Royal London Hospital (Part B/C)

    Whitechapel, United Kingdom

  • Tulane University Medical Center (Part B/C)

    New Orleans, Louisiana, 70112, United States

  • Universitair Medisch Centrum Utrecht (Part B/C)

    Utrecht, Netherlands

  • University Hospital Leuven - Campus Gasthuisberg (Part B/C)

    Leuven, Belgium

  • University of California, San Diego (UCSD) (Part B/C)

    La Jolla, California, 92093, United States

  • Washington Institute for Coagulation (Part B/C)

    Seattle, Washington, 98101, United States

Conditions

Explore the condition pages connected to this study.