Scientists seek answers for rare, deadly pigment disorder

NCT ID NCT00001456

First seen Nov 01, 2025 · Last updated May 16, 2026 · Updated 22 times

Summary

This study aims to learn more about Hermansky-Pudlak Syndrome (HPS), a rare inherited disease that causes light skin and hair, bleeding problems, and can lead to deadly lung scarring. Researchers will evaluate up to 600 patients of all backgrounds to track the disease's course and find its genetic causes. No new treatments are being tested; the goal is to gather information to better understand HPS.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • National Institutes of Health Clinical Center

    RECRUITING

    Bethesda, Maryland, 20892, United States

Conditions

Explore the condition pages connected to this study.