Scientists track rare genetic disease to unlock its secrets

NCT ID NCT07213297

Summary

This study aims to better understand hereditary transthyretin amyloidosis, a rare genetic disease where abnormal protein deposits damage organs over time. Researchers will follow 20 adults with confirmed genetic mutations to track how their symptoms develop and change. The study involves regular check-ups and tests to identify patterns in how the disease affects the heart, nerves, and other body systems.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Hospital Cuenca Alta de Cañuelas

    RECRUITING

    Cañuelas, Buenos Aires, 1814, Argentina

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.