One-Shot gene therapy aims to free patients from lifelong bleeding disorder treatments

NCT ID NCT06700096

Summary

This study is testing whether a single dose of an experimental gene therapy called ANB-002 can control bleeding as well as, or better than, the standard preventive injections of clotting factor (FIX) in adults with severe hemophilia B. Participants will first be monitored for 6 months while on their standard treatment, then receive the one-time gene therapy infusion and be followed for up to 5 years. The main goal is to see if the therapy reduces the annual rate of bleeding episodes.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Almazov National Medical Research Centre

    RECRUITING

    Saint Petersburg, 197341, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Chelyabinsk Regional Clinical Hospital

    RECRUITING

    Chelyabinsk, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Federal Budgetary Institution "Moscow City Clinical Hospital named after S. P. Botkin"

    RECRUITING

    Moscow, 125284, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Federal State Budgetary Educational Institution of Higher Education "Bashkir State Medical University" of the Ministry of Healthcare of the Russian Federation

    RECRUITING

    Ufa, 450008, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Federal State Budgetary Educational Institution of Higher Education "Samara State Medical University" of the Ministry of Healthcare of the Russian Federation

    RECRUITING

    Samara, 443099, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Federal State Budgetary Institution "National Medical Research Centre for Hematology" of the Ministry of Health of Russian Federation (Department of Clinical Diagnostics for Hematology and Hemostasis Disorders)

    RECRUITING

    Moscow, 125167, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Federal State Budgetary Institution "National Medical Research Centre for Hematology" of the Ministry of Health of Russian Federation (Department of Traumatology and Reconstructive and Restorative Orthopedics for Patients with Hemophilia)

    RECRUITING

    Moscow, 125167, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Federal State Budgetary Organization of Science "Kirov Research Institute of Hematology and Blood Transfusions of Federal Medical Biological agency"

    RECRUITING

    Kirov, 610027, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • King Chulalongkorn Memorial Hospital

    NOT_YET_RECRUITING

    Bangkok, 10330, Thailand

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Ramathibodi Hospital

    NOT_YET_RECRUITING

    Bangkok, 10400, Thailand

    Contact Email: •••••@•••••

  • Russian Research Institute of Hematology and Transfusiology Federal State Institution of Federal Medical and Biological Agency

    RECRUITING

    Saint Petersburg, 193024, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Siriraj Hospital

    NOT_YET_RECRUITING

    Bangkok, 10700, Thailand

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • State Novosibirsk Regional Clinical Hospital

    RECRUITING

    Novosibirsk, 630087, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • State budgetary healthcare institution Leningrad Regional Clinical Hospital

    RECRUITING

    Saint Petersburg, 188663, Russia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.