Tracking new hemophilia treatments in children and First-Time patients
NCT ID NCT03695978
Summary
This study follows 200 patients with severe hemophilia A who are just starting treatment with one of three specific clotting factor products. Researchers will observe how well these treatments control bleeding in real-world settings and monitor for safety issues, particularly focusing on children and patients with minimal prior treatment. The goal is to gather practical information about how these medications work outside of controlled clinical trials.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Azerbaijan State Advanced Training Institute for Doctors Hematology Department Scientific-Research Center of Hemophilia
WITHDRAWNBaku, AZ1012, Azerbaijan
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Azienda Ospedaliera-Universitaria Policlinico "Vittorio Emanuele", Centro di Riferimento Regionale per la Prevenzione, Diagnosi e Cura delle Malattie Rare della Coagulazione nel Bambino e neel'Adulto. U.O.C Ematologia con trapianto di Midollo Osseo
RECRUITINGCatania, 95123, Italy
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Azienda Ospedaliero Universitaria Careggi
RECRUITINGFlorence, 50134, Italy
Contact Email: •••••@•••••
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Birmingham Children's Hospital NHS Foundation Trust
WITHDRAWNBirmingham, B46NH, United Kingdom
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C.tro Emofilia A.O. Città della salute e della scienza di Torino, Ospedale Regina Margherita
RECRUITINGTorino, Italy
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CENIDOR
ACTIVE_NOT_RECRUITINGSalta, Argentina
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CENTRE HOSPITALIER UNIVERSITAIRE de BESANCON
RECRUITINGBesançon, France
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CHRU Hopital Nord, Secretariat de pediatre, bat E niv +3
RECRUITINGSaint-Priest-en-Jarez, 42270, France
Contact Email: •••••@•••••
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CHRU Tours - Hôpital Trousseau
RECRUITINGChambray-lès-Tours, France
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CHU Hotel Dieu, Centre de Traitment de l'Hemophilie
RECRUITINGNantes, 44093, France
Contact Email: •••••@•••••
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Center for Thrombosis and Hemorrhagic Diseases, IRCCS Humanitas Research Hospital
RECRUITINGMilan, Italy
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Centre Régional de Traitement de l'hémophilie
RECRUITINGLe Mans, France
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Centro Emofilia - AUO di Padova
WITHDRAWNPadua, Italy
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Children's Hospital Affiliate of Vilnius Universtity Hospital Santaros Klinikos
RECRUITINGVilnius, LT-08406, Lithuania
Contact Email: •••••@•••••
Contact Email: •••••@•••••
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Cliniques Universitaires Saint-Luc
RECRUITINGBrussels, 1200, Belgium
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Cliniques Universitaires Saint-Luc
RECRUITINGBrussels, 1200, Belgium
Contact Email: •••••@•••••
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Coagulation Research Centre GmbH
RECRUITINGDuisburg, 47051, Germany
Contact Email: •••••@•••••
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Cure 4 The Kids Foundation Children's Specialty Center
WITHDRAWNLas Vegas, Nevada, 89109, United States
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Department of Hematology Research Research Transition Facility
COMPLETEDEdmonton, T6G 2V2, Canada
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Great Ormond Street Hospital for Children NHS Trust, Haemophilia Centre
RECRUITINGLondon, WC1N 3JH, United Kingdom
Contact Email: •••••@•••••
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HRU Malaga
NOT_YET_RECRUITINGMálaga, Spain
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HZRM GmbH
ACTIVE_NOT_RECRUITINGFrankfurt, Germany
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Heim Pál National Pediatric Institute Department of Oncology and Hematology
RECRUITINGBudapest, 1089, Hungary
Contact
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Hopital Simone Veil Groupement Hospitalier Eaubonne-Montmorency
RECRUITINGMontmorency, 95160, France
Contact Email: •••••@•••••
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Hospital General Universitario de Alicante Hematología y Hemoterapia
RECRUITINGAlicante, 03010, Spain
Contact Email: •••••@•••••
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Hospital Infantil de Morelia Eva Sámano de López Mateos
RECRUITINGMorelia, Mexico
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Hospital Universitari Vall D'Hebrón, Unitat d'Hemofilia
RECRUITINGBarcelona, 02035, Spain
Contact Email: •••••@•••••
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Hospital Universitario Dr. José Eleuterio Gonzalez S/N
RECRUITINGNuevo León, Mexico
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Hospital Universitario y Politécnico La Fe
ACTIVE_NOT_RECRUITINGValencia, Spain
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Hôpital Universitaire des Enfants Reine Fabiola
RECRUITINGBrussels, 1020, Belgium
Contact Email: •••••@•••••
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Hôspital Necker Enfants Malades
RECRUITINGParis, France
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Institute of Experimental Haematology and Transfusion Medicine (IHT) University Clinic Bonn (AöR)
RECRUITINGBonn, 53127, Germany
Contact Email: •••••@•••••
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Istanbul University Faculty of Medicine
WITHDRAWNFatih, Turkey (Türkiye)
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John Radcliffe Hospital, Oxford University Hospitals, NHS Foundation Trust
RECRUITINGHeadington, Oxford, OX3 9DU, United Kingdom
Contact Email: •••••@•••••
Contact Email: •••••@•••••
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McMaster University, Division of Pediatric Hematology/Oncology Room 3N27
WITHDRAWNHamilton, Ontario, 1800NOCLOTS, Canada
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Moscow State Government-financed Public Healthcare Institution "Morozovskaya Children Clinical Hospital of Moscow Healthcare Department"
WITHDRAWNMoscow, 119049, Russia
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Newcastle Haemophilia Comprehensive Care Centre, Royal Victoria Infirmary
RECRUITINGNewcastle upon Tyne, NE1 4LP, United Kingdom
Contact Email: •••••@•••••
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Ochsner Clinic Foundation
RECRUITINGNew Orleans, Louisiana, 70121, United States
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Ospedale Maggiore Policlinico
RECRUITINGMilan, 920122, Italy
Contact Email: •••••@•••••
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Ospedale Pediatrico "Giovani XXIII"
RECRUITINGBari, Italy
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Ospedale Regina Margherita
WITHDRAWNTurin, 10126, Italy
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Ospedale San Giacomo
COMPLETEDCastelfranco Veneto, 31033, Italy
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Policlinico Sant'Orsola Malpighi
RECRUITINGBologna, 40138, Italy
Contact Email: •••••@•••••
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Policlinico Umberto I
RECRUITINGRome, 00161, Italy
Contact Email: •••••@•••••
Contact Email: •••••@•••••
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Republican Scientific Center for Radiation Medicine and Human Ecology
WITHDRAWNHomyel, 246040, Belarus
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Republican Scientific and Practical Centre of Children Oncology, Hematology and Immunology
RECRUITINGMinsk, 223053, Belarus
Contact Email: •••••@•••••
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SMO and Scientific Services S.A.P.P de C.V
RECRUITINGNuevo León, Mexico
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Saint-Petersburg State Budget Healthcare Institution "City Out-patient Clinical # 37"
WITHDRAWNSaint Petersburg, 191186, Russia
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Tallinn Childrenś Hospital Clinic of Paediatric Department of Haematology and Oncology
WITHDRAWNTallinn, 13419, Estonia
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Universitary Hospital Son Espases (Hematology Service)
ACTIVE_NOT_RECRUITINGPalma de Mallorca, Spain
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University Hospital Centre Zagreb
RECRUITINGZagreb, Croatia
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University Hospital Essen
ACTIVE_NOT_RECRUITINGEssen, Germany
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University of Debrecen Department of Pediatrics
RECRUITINGDebrecen, 4032, Hungary
Contact
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University of Miami Miller School of Medicine
ACTIVE_NOT_RECRUITINGMiami, Florida, 33136, United States
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Vivantes - Netzwerk für Gesundheit GmbH Klinikum im Friedrichshain
ACTIVE_NOT_RECRUITINGBerlin, 10249, Germany
Conditions
Explore the condition pages connected to this study.