Tracking new hemophilia treatments in children and First-Time patients

NCT ID NCT03695978

Summary

This study follows 200 patients with severe hemophilia A who are just starting treatment with one of three specific clotting factor products. Researchers will observe how well these treatments control bleeding in real-world settings and monitor for safety issues, particularly focusing on children and patients with minimal prior treatment. The goal is to gather practical information about how these medications work outside of controlled clinical trials.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Azerbaijan State Advanced Training Institute for Doctors Hematology Department Scientific-Research Center of Hemophilia

    WITHDRAWN

    Baku, AZ1012, Azerbaijan

  • Azienda Ospedaliera-Universitaria Policlinico "Vittorio Emanuele", Centro di Riferimento Regionale per la Prevenzione, Diagnosi e Cura delle Malattie Rare della Coagulazione nel Bambino e neel'Adulto. U.O.C Ematologia con trapianto di Midollo Osseo

    RECRUITING

    Catania, 95123, Italy

  • Azienda Ospedaliero Universitaria Careggi

    RECRUITING

    Florence, 50134, Italy

    Contact Email: •••••@•••••

  • Birmingham Children's Hospital NHS Foundation Trust

    WITHDRAWN

    Birmingham, B46NH, United Kingdom

  • C.tro Emofilia A.O. Città della salute e della scienza di Torino, Ospedale Regina Margherita

    RECRUITING

    Torino, Italy

  • CENIDOR

    ACTIVE_NOT_RECRUITING

    Salta, Argentina

  • CENTRE HOSPITALIER UNIVERSITAIRE de BESANCON

    RECRUITING

    Besançon, France

  • CHRU Hopital Nord, Secretariat de pediatre, bat E niv +3

    RECRUITING

    Saint-Priest-en-Jarez, 42270, France

    Contact Email: •••••@•••••

  • CHRU Tours - Hôpital Trousseau

    RECRUITING

    Chambray-lès-Tours, France

  • CHU Hotel Dieu, Centre de Traitment de l'Hemophilie

    RECRUITING

    Nantes, 44093, France

    Contact Email: •••••@•••••

  • Center for Thrombosis and Hemorrhagic Diseases, IRCCS Humanitas Research Hospital

    RECRUITING

    Milan, Italy

  • Centre Régional de Traitement de l'hémophilie

    RECRUITING

    Le Mans, France

  • Centro Emofilia - AUO di Padova

    WITHDRAWN

    Padua, Italy

  • Children's Hospital Affiliate of Vilnius Universtity Hospital Santaros Klinikos

    RECRUITING

    Vilnius, LT-08406, Lithuania

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • Cliniques Universitaires Saint-Luc

    RECRUITING

    Brussels, 1200, Belgium

  • Cliniques Universitaires Saint-Luc

    RECRUITING

    Brussels, 1200, Belgium

    Contact Email: •••••@•••••

  • Coagulation Research Centre GmbH

    RECRUITING

    Duisburg, 47051, Germany

    Contact Email: •••••@•••••

  • Cure 4 The Kids Foundation Children's Specialty Center

    WITHDRAWN

    Las Vegas, Nevada, 89109, United States

  • Department of Hematology Research Research Transition Facility

    COMPLETED

    Edmonton, T6G 2V2, Canada

  • Great Ormond Street Hospital for Children NHS Trust, Haemophilia Centre

    RECRUITING

    London, WC1N 3JH, United Kingdom

    Contact Email: •••••@•••••

  • HRU Malaga

    NOT_YET_RECRUITING

    Málaga, Spain

  • HZRM GmbH

    ACTIVE_NOT_RECRUITING

    Frankfurt, Germany

  • Heim Pál National Pediatric Institute Department of Oncology and Hematology

    RECRUITING

    Budapest, 1089, Hungary

    Contact

  • Hopital Simone Veil Groupement Hospitalier Eaubonne-Montmorency

    RECRUITING

    Montmorency, 95160, France

    Contact Email: •••••@•••••

  • Hospital General Universitario de Alicante Hematología y Hemoterapia

    RECRUITING

    Alicante, 03010, Spain

    Contact Email: •••••@•••••

  • Hospital Infantil de Morelia Eva Sámano de López Mateos

    RECRUITING

    Morelia, Mexico

  • Hospital Universitari Vall D'Hebrón, Unitat d'Hemofilia

    RECRUITING

    Barcelona, 02035, Spain

    Contact Email: •••••@•••••

  • Hospital Universitario Dr. José Eleuterio Gonzalez S/N

    RECRUITING

    Nuevo León, Mexico

  • Hospital Universitario y Politécnico La Fe

    ACTIVE_NOT_RECRUITING

    Valencia, Spain

  • Hôpital Universitaire des Enfants Reine Fabiola

    RECRUITING

    Brussels, 1020, Belgium

    Contact Email: •••••@•••••

  • Hôspital Necker Enfants Malades

    RECRUITING

    Paris, France

  • Institute of Experimental Haematology and Transfusion Medicine (IHT) University Clinic Bonn (AöR)

    RECRUITING

    Bonn, 53127, Germany

    Contact Email: •••••@•••••

  • Istanbul University Faculty of Medicine

    WITHDRAWN

    Fatih, Turkey (Türkiye)

  • John Radcliffe Hospital, Oxford University Hospitals, NHS Foundation Trust

    RECRUITING

    Headington, Oxford, OX3 9DU, United Kingdom

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • McMaster University, Division of Pediatric Hematology/Oncology Room 3N27

    WITHDRAWN

    Hamilton, Ontario, 1800NOCLOTS, Canada

  • Moscow State Government-financed Public Healthcare Institution "Morozovskaya Children Clinical Hospital of Moscow Healthcare Department"

    WITHDRAWN

    Moscow, 119049, Russia

  • Newcastle Haemophilia Comprehensive Care Centre, Royal Victoria Infirmary

    RECRUITING

    Newcastle upon Tyne, NE1 4LP, United Kingdom

    Contact Email: •••••@•••••

  • Ochsner Clinic Foundation

    RECRUITING

    New Orleans, Louisiana, 70121, United States

  • Ospedale Maggiore Policlinico

    RECRUITING

    Milan, 920122, Italy

    Contact Email: •••••@•••••

  • Ospedale Pediatrico "Giovani XXIII"

    RECRUITING

    Bari, Italy

  • Ospedale Regina Margherita

    WITHDRAWN

    Turin, 10126, Italy

  • Ospedale San Giacomo

    COMPLETED

    Castelfranco Veneto, 31033, Italy

  • Policlinico Sant'Orsola Malpighi

    RECRUITING

    Bologna, 40138, Italy

    Contact Email: •••••@•••••

  • Policlinico Umberto I

    RECRUITING

    Rome, 00161, Italy

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • Republican Scientific Center for Radiation Medicine and Human Ecology

    WITHDRAWN

    Homyel, 246040, Belarus

  • Republican Scientific and Practical Centre of Children Oncology, Hematology and Immunology

    RECRUITING

    Minsk, 223053, Belarus

    Contact Email: •••••@•••••

  • SMO and Scientific Services S.A.P.P de C.V

    RECRUITING

    Nuevo León, Mexico

  • Saint-Petersburg State Budget Healthcare Institution "City Out-patient Clinical # 37"

    WITHDRAWN

    Saint Petersburg, 191186, Russia

  • Tallinn Childrenś Hospital Clinic of Paediatric Department of Haematology and Oncology

    WITHDRAWN

    Tallinn, 13419, Estonia

  • Universitary Hospital Son Espases (Hematology Service)

    ACTIVE_NOT_RECRUITING

    Palma de Mallorca, Spain

  • University Hospital Centre Zagreb

    RECRUITING

    Zagreb, Croatia

  • University Hospital Essen

    ACTIVE_NOT_RECRUITING

    Essen, Germany

  • University of Debrecen Department of Pediatrics

    RECRUITING

    Debrecen, 4032, Hungary

    Contact

  • University of Miami Miller School of Medicine

    ACTIVE_NOT_RECRUITING

    Miami, Florida, 33136, United States

  • Vivantes - Netzwerk für Gesundheit GmbH Klinikum im Friedrichshain

    ACTIVE_NOT_RECRUITING

    Berlin, 10249, Germany

Conditions

Explore the condition pages connected to this study.