5-Year watch: can new hemophilia drug save Patients' joints?

NCT ID NCT05911763

Summary

This study aims to see how well a new treatment, efanesoctocog alfa, works over five years to protect the joints of people with Hemophilia A. It will follow 200 patients in the US and Japan who are already receiving this treatment as part of their standard care. The main goal is to measure changes in joint bleeding rates and joint health to understand the treatment's real-world effectiveness and safety.

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Contacts and locations

Locations

  • Banner MD Anderson Cancer Center- Site Number : 8400008

    Gilbert, Arizona, 85234-2165, United States

  • Blood Center of Wisconnsin- Site Number : 8400027

    Milwaukee, Wisconsin, 53233-2121, United States

  • Children's Specialty Center - Las Vegas- Site Number : 8400007

    Las Vegas, Nevada, 89109, United States

  • Cincinnati Children's Hospital Medical Center - PIN- Site Number : 8400006

    Cincinnati, Ohio, 45229-3026, United States

  • Dana Farber and Boston Children's Hospital- Site Number : 8400031

    Boston, Massachusetts, 02215-5418, United States

  • Gulf States Hemophilia and Thrombophilia Center- Site Number : 8400029

    Houston, Texas, 77030, United States

  • Hemophilia Center of Western Pennsylvania- Site Number : 8400012

    Pittsburgh, Pennsylvania, 15213-4306, United States

  • Indiana Hemophilia and Thrombosis Center- Site Number : 8400013

    Indianapolis, Indiana, 46260-1920, United States

  • Johns Hopkins All Childrens Hospital - Outpatient Care Center - PIN- Site Number : 8400025

    St. Petersburg, Florida, 33701-4804, United States

  • Loma Linda University- Site Number : 8400015

    Loma Linda, California, 92354-3450, United States

  • M Health Fairview- Masonic Cancer Clinic - Clinics- Site Number : 8400010

    Minneapolis, Minnesota, 55455-4800, United States

  • Mayo Clinic - PPDS- Site Number : 8400035

    Rochester, Minnesota, 55905-0001, United States

  • Mississippi Center For Advanced Medicine - 7731 Old Canton Rd- Site Number : 8400016

    Madison, Mississippi, 39110-6115, United States

  • Orthopedic Institute for Children- Site Number : 8400004

    Los Angeles, California, 90007, United States

  • Rush University Medical Center -1725 W Harrison St- Site Number : 8400014

    Chicago, Illinois, 60612-3863, United States

  • The Bleeding and Clotting Disorders Institute- Site Number : 8400005

    Peoria, Illinois, 61615, United States

  • The Center for Inherited Blood Disorders- Site Number : 8400001

    Orange, California, 92868, United States

  • University Of Iowa Hospitals And Clinics- Site Number : 8400026

    Iowa City, Iowa, 52242-1009, United States

  • University of Colorado Hemophilia and Thrombosis Center- Site Number : 8400019

    Aurora, Colorado, 80045-7202, United States

  • University of Michigan Hospital - 1500 E Medical Center Dr- Site Number : 8400023

    Ann Arbor, Michigan, 48109-5000, United States

  • University of Nebraska Medical Center - 985400 Nebraska Medical Center- Site Number : 8400009

    Omaha, Nebraska, 68114-4113, United States

  • University of Texas Southwestern Medical Center- Site Number : 8400011

    Dallas, Texas, 75390-8565, United States

  • University of Texas Southwestern Medical Center-2001 Inwood Rd- Site Number : 8400020

    Dallas, Texas, 75390-7202, United States

  • Vanderbilt University Medical Center- Site Number : 8400003

    Nashville, Tennessee, 37232-0011, United States

  • Washington Institute for Coagulation- Site Number : 8400022

    Seattle, Washington, 98101-3932, United States

  • Weill Cornell Medicine-New York Presbyterian Hospital- Site Number : 8400021

    New York, New York, 10065-4870, United States

  • William A. Shands Hospital at the University of Florida- Site Number : 8400032

    Gainesville, Florida, 32610-3003, United States

  • ~Massachusetts General Hospital- Site Number : 8400017

    Boston, Massachusetts, 02114, United States

Conditions

Explore the condition pages connected to this study.