Gene therapy trial seeks to free hemophilia patients from frequent injections

NCT ID NCT07226206

Summary

This early-stage study is testing the safety of an experimental gene therapy called SPK-8011QQ in adult men with severe hemophilia A. The main goal is to see if the treatment is safe and well-tolerated, not to prove it works. Researchers will carefully monitor five participants for any side effects after they receive a single dose of the therapy.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Kaiser Permanente

    Vallejo, California, 94589-2441, United States

Conditions

Explore the condition pages connected to this study.