New drug trial offers hope for angelman syndrome
NCT ID NCT07157254
Summary
This study is testing an experimental drug called GTX-102 in people with Angelman syndrome, a rare genetic disorder that affects development and causes seizures and movement problems. Researchers want to see if the drug is safe and if it can improve thinking, communication, behavior, and motor skills. The trial includes 60 children and adults, divided into groups based on their age and specific genetic type of Angelman syndrome.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Akron Children's Hospital
RECRUITINGAkron, Ohio, 44308, United States
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Azienda Ospedaliera Universitaria Meyer IRCCS
RECRUITINGFlorence, Italy
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Carum Research Inc.
RECRUITINGDallas, Texas, 75243, United States
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Clinical Trial Site
NOT_YET_RECRUITINGLos Angeles, California, 90048, United States
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Clinical Trial Site
NOT_YET_RECRUITINGBaltimore, Maryland, 21205, United States
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Clinical Trial Site
NOT_YET_RECRUITINGKansas City, Missouri, 64108, United States
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Clinical Trial Site
NOT_YET_RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
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Clinical Trial Site
NOT_YET_RECRUITINGPilar, Buenos Aires, Argentina
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Clinical Trial Site
NOT_YET_RECRUITINGCuritiba, Paraná, Brazil
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Clinical Trial Site
NOT_YET_RECRUITINGSanta Cecília, Porto Alegre, Brazil
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Clinical Trial Site
NOT_YET_RECRUITINGMarseille, France
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Clinical Trial Site
NOT_YET_RECRUITINGParis, France
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Clinical Trial Site
NOT_YET_RECRUITINGRamat Gan, Israel
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Clinical Trial Site
NOT_YET_RECRUITINGRome, Italy
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Clinical Trial Site
NOT_YET_RECRUITINGLondon, United Kingdom
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Clinical Trial Site
NOT_YET_RECRUITINGOxford, United Kingdom
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Fondazione IRCCS Istituto Neurologico C. Besta
RECRUITINGMilan, Italy
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Hospital Santa Joao
RECRUITINGPorto, Portugal
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Hospital de Santa Maria
RECRUITINGLisbon, Portugal
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Rare Disease Research
RECRUITINGHillsborough, North Carolina, 27278, United States
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Rush University Medical Center
RECRUITINGChicago, Illinois, 60612, United States
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UT Health Austin
RECRUITINGAustin, Texas, 78723, United States
Conditions
Explore the condition pages connected to this study.