New drug aims to help kids with dwarfism grow taller
NCT ID NCT03424018
Summary
This study is testing the long-term safety and effectiveness of an experimental drug called BMN 111 in children with achondroplasia, the most common form of dwarfism. The main goal is to see if the drug can safely increase the children's annual growth rate over many years. Researchers will also measure if the treatment improves daily activities and quality of life as the children grow into adulthood.
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Contacts and locations
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Locations
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Acibadem University School of Medicine
Istanbul, 34752, Turkey (Türkiye)
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Alfred I. duPont Hospital for Children
Wilmington, Delaware, 19803, United States
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Ann and Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, 60611, United States
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Baylor College of Medicine
Houston, Texas, 77030, United States
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Children's Hospital & Research Center Oakland
Oakland, California, 94609, United States
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Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, 45229, United States
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Emory University
Atlanta, Georgia, 30322, United States
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Guy's and St. Thomas NHS Foundation Trust Evelina Children's Hospital
London, SE1 9RT, United Kingdom
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Harbor - UCLA Medical Center
Torrance, California, 90509, United States
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Hospital Sant Joan de Deu
Barcelona, 08950, Spain
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Hospital Universitario Virgen de la Victoria
Málaga, 29010, Spain
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Institut Catala de Traumatologica I Medicina de l'Esport
Barcelona, 08028, Spain
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Johns Hopkins University
Baltimore, Maryland, 21287, United States
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Medical College of Wisconsin, Children's Hospital
Milwaukee, Wisconsin, 53226, United States
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Murdoch Children's Research Institute
Parkville, Victoria, 3052, Australia
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Osaka University Hospital
Osaka, Japan
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Otto-von-Gericke Universitaet, Universitaetskinderklinik
Magdeburg, 39120, Germany
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Saitama Children's Medical Center
Saitama, Japan
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Seattle Children's Hospital
Seattle, Washington, 98105, United States
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Sheffield Children's NHS Foundation Trust
Sheffield, S10 2TH, United Kingdom
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The Children's Hospital at Westmead
Westmead, New South Wales, 2145, Australia
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Tokushima University Hospital
Tokushima, Japan
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University of Missouri
Columbia, Missouri, 65201, United States
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Universitätsklinikum Münster
Münster, 48149, Germany
Conditions
Explore the condition pages connected to this study.