Promising drug takes on rare nerve disorder in major new trial

NCT ID NCT07191912

First seen Nov 01, 2025 · Last updated May 17, 2026 · Updated 25 times

Summary

This study tests a drug called govorestat against a placebo in 155 people aged 16-65 with a rare inherited nerve disease (CMT-SORD) that causes weakness and trouble walking. The goal is to see if the drug improves daily function and walking speed over up to 36 months. Participants will not know if they receive the drug or placebo.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • CHU La Timone

    Marseille, 13005, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Carlo Besta Neurological Institute

    Milan, 20133, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Charité - Universitätsmedizin Berlin

    Berlin, 10117, Germany

  • Clinic for Special Children

    Gordonville, Pennsylvania, 17529, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Institut de Myologie

    Paris, 75013, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Istanbul University

    Istanbul, 34093, Turkey (Türkiye)

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Koç University Hospital

    Istanbul, 34010, Turkey (Türkiye)

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • La Fe University and Polytechnic Hospital

    Valencia, 46026, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Sydney Childrens

    Sydney, 2013, Australia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Uniklinik of the RWTH Aachen University

    Aachen, 52074, Germany

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University Medicine Gottingen (UMG)

    Göttingen, 37075, Germany

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University of Iowa

    Iowa City, Iowa, 52242, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Vall d'Hebron Institut de Recerca (VHIR)

    Barcelona, 08035, Spain

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.