Scientists hunt for 'Modifier Genes' that could explain why some LMNA patients fare better than others

NCT ID NCT05394506

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study aims to identify genetic factors that affect how severe muscle and heart problems become in people with LMNA gene mutations. Researchers will collect skin and muscle samples from 40 participants and use advanced DNA and RNA analysis to look for protective or aggravating genes. No treatment is being tested; the goal is to better understand why symptoms vary so widely among patients.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

What this could lead to

If successful, this could identify genes that make laminopathy milder or worse, pointing toward future targets for therapies.

What could go wrong

This is a small, early observational study (40 participants) that does not test any treatment. It may not find clear genetic modifiers, and results may not apply to all patients.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Autosomal Emery-Dreifuss Muscular Dystrophy congenital muscular dystrophy due to LMNA mutation dilated cardiomyopathy dilated cardiomyopathy 1A Emery-Dreifuss muscular dystrophy Emery-Dreifuss muscular dystrophy 2, autosomal dominant laminopathy muscular dystrophy

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Centre de référence maladies neuromusculaires, Hôpital Femme Mère Enfant, CHU Lyon

    RECRUITING

    Bron, Auvergne-Rhône-Alpes, 69677, France

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • Centre de référence maladies neuromusculaires, Institut de myologie, Hôpital Pitié-Salpêtrière

    RECRUITING

    Paris, France, 75013, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Email: •••••@•••••

  • Centre de référence pour les maladies cardiaques héréditaires

    RECRUITING

    Paris, Paris, 75013, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Laboratoire d'Explorations Fonctionnelles - Centre de Référence Maladies Neuromusculaires Rares, CHU Nantes

    NOT_YET_RECRUITING

    Nantes, Loire-Atlantique, 44093, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Service de Génétique médicale, CHU Rennes

    NOT_YET_RECRUITING

    Rennes, Ille-et-Vilaine, 35000, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Service de Neurologie, Réanimation Pédiatriques, Hôpital Raymond Poincaré, Hôpitaux Universitaires, Paris-Ile-de-France-Ouest

    NOT_YET_RECRUITING

    Garches, Île-de-France Region, 92380, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Service de Neuropédiatrie, Centre de Référence Maladies Neuromusculaires, CHU de Montpellier

    NOT_YET_RECRUITING

    Montpellier, Hérault, 34295, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Service de cardiologie & Service de Neurophysiologie - CHU de Rouen

    RECRUITING

    Rouen, Normandy, 76031, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••