Gene therapy trial offers hope for healing 'Butterfly Skin' wounds

NCT ID NCT04213261

Summary

This study is testing whether a new gene therapy called FCX-007 can help heal wounds in people with recessive dystrophic epidermolysis bullosa (RDEB), a painful and severe genetic condition that causes fragile, blistering skin. The therapy involves taking a patient's own skin cells, modifying them with a corrective gene, and injecting them back into specific wounds. The main goal is to see if these treated wounds heal better than untreated wounds over 24 weeks.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Dell Children's Medical Group

    Austin, Texas, 78723, United States

  • Mayo Clinic

    Rochester, Minnesota, 55905, United States

  • Solutions Through Advanced Research, Inc.

    Jacksonville, Florida, 32256, United States

  • Stanford University

    Stanford, California, 94305, United States

Conditions

Explore the condition pages connected to this study.