One-Shot gene therapy aims to free patients from sickle cell crises

NCT ID NCT06565026

First seen Feb 14, 2026 · Last updated Apr 16, 2026 · Updated 5 times

Summary

This early study is testing a one-time treatment for severe sickle cell disease. Doctors take a patient's own blood stem cells, edit their genes in a lab to boost protective fetal hemoglobin, and then return them. The goal is to see if this single treatment is safe and can reduce or eliminate painful sickle cell crises for at least a year.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • The First Affiliated Hospital of Guangxi Medical University

    RECRUITING

    Nanning, Guangxi, China

    Contact

    Contact

Conditions

Explore the condition pages connected to this study.