One-Shot gene therapy aims to cure devastating baby immune disease

NCT ID NCT03217617

Summary

This trial is testing a one-time gene therapy for babies with a severe, often fatal genetic immune disorder called SCID-X1. Doctors give a single IV infusion containing a corrected gene to try to fix the immune system. The goal is to see if this treatment is safe and can help these children develop a working immune system to fight off infections.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Guilin Hospital of Chinese Traditional and Western Medicine

    RECRUITING

    Guilin, Guangxi, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Shenzhen Geno-immune Medical Institute

    RECRUITING

    Shenzhen, Guangdong, 518000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.