Doctors test One-Shot gene injection to fight rare blindness

NCT ID NCT05616793

Summary

This study is testing a new gene therapy called OPGx-001 for people with LCA5, a rare genetic condition that damages the retina and leads to vision loss. A small number of participants will receive an injection of the therapy into one eye to see if it is safe and if it might help preserve or improve vision. The study will also follow a group of untreated patients for 6 months to better understand how the disease naturally progresses.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Retina Foundation of the Southwest

    RECRUITING

    Dallas, Texas, 75231, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of Pennsylvania Perelman School of Medicine

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.