Gene injection aims to restore vision in inherited blindness trial

NCT ID NCT07054632

Summary

This study is testing whether a one-time gene therapy injection (called LX101) can improve vision in people with a specific inherited retinal disease that causes blindness. The trial involves 30 participants, aged 6 and older, who have vision loss due to mutations in the RPE65 gene. Participants are randomly assigned to either receive the gene therapy injection or no treatment, so researchers can compare outcomes.

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Contacts and locations

Locations

  • Shanghai General Hospital

    Shanghai, China

  • Southwest Hospital of AMU

    Chongqing, China

  • Tianjin Medical University Ophthalmology Hospital

    Tianjin, China

  • Zhongshan Ophthalmic Center, Sun Yat sen University

    Guangzhou, Guangdong, China

Conditions

Explore the condition pages connected to this study.