One-Shot gene therapy aims to free patients from lifelong injections

NCT ID NCT06111638

Summary

This study is testing a single injection of an experimental gene therapy called BBM-H803 for adults with severe Hemophilia A. The goal is to see if the treatment is safe and if it can help the body produce its own missing clotting factor, which could reduce or prevent bleeding episodes. Researchers will monitor participants for side effects and measure how well the therapy controls bleeding over time.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Affiliated Hospital of Guizhou Medical University

    RECRUITING

    Guiyang, Guizhou, 550001, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Institute of Hematology & Blood Diseases Hospital Chinese Academy of Medical Sciences & Peking Union Medical College

    RECRUITING

    Tianjin, Tianjin Municipality, 300020, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Peking Union Medical College Hospital, Chinese Academy of Medical Sciences

    RECRUITING

    Beijing, Beijing Municipality, 100005, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Sichuan Provincial People's Hospital

    RECRUITING

    Chengde, Sichuan, 610031, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Southern Hospital, Southern Medical University

    RECRUITING

    Guangzhou, Guangdong, 510515, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Affiliated Hospital of Northwest University Xi'an No.3 Hospital

    RECRUITING

    Xi’an, Shanxi, 710000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The First Affiliated Hospital of Soochow University

    RECRUITING

    Suzhou, Jiangsu, 215006, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Second Affiliated Hospital of Kunming Medical University

    RECRUITING

    Kunming, Yunnan, 650032, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Wuhan Union Hospital Affiliated to Huazhong University of Science and Technology

    RECRUITING

    Wuhan, Hubei, 430000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Xiangya Hospital Central South University

    RECRUITING

    Changsha, Hunan, 410008, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.