One-Time shot aims to restore hearing in deafness caused by gene fault

NCT ID NCT05821959

Summary

This early-stage trial is testing a one-time gene therapy for people born with profound hearing loss due to specific mutations in the otoferlin gene. Researchers will inject a modified virus carrying a corrected gene directly into the inner ear during surgery to see if it's safe and if it can help restore hearing. The study will also test a special device designed to deliver the therapy precisely.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19146, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Cincinnati Children's Hospital Medical Center

    RECRUITING

    Cincinnati, Ohio, 45229, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • National Taiwan University Hospital

    RECRUITING

    Taipei, 100, Taiwan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Hospital for Sick Children [email protected] +1 (416) 813 6683

    RECRUITING

    Toronto, Ontario, M5G 1X8, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University College London

    RECRUITING

    London, United Kingdom, NW1 2PG, United Kingdom

    Contact Email: •••••@•••••

  • University of California, San Francisco Benioff Children's Hospital

    RECRUITING

    San Francisco, California, 94158, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of Iowa

    RECRUITING

    Iowa City, Iowa, 52242, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Vanderbilt Bill Wilkerson Center

    RECRUITING

    Nashville, Tennessee, 37232, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.