First-in-Human gene therapy tested for blinding eye disease

NCT ID NCT07311863

Summary

This is a very early study to check if a new gene therapy called UGX202 is safe for people with advanced retinitis pigmentosa (RP), a disease that causes severe vision loss. Six patients with very low vision will receive a single injection of the therapy into one eye and be monitored for a year. The main goal is to see if the treatment is safe, while also looking for any early signs that it might help preserve or improve vision.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Eye & ENT Hospital of Fudan University

    Shanghai, Shanghai Municipality, 200031, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.