Gene therapy offers hope for rare blindness

NCT ID NCT07054632

First seen Mar 10, 2026 · Last updated May 17, 2026 · Updated 7 times

Summary

This study tests a gene therapy called LX101 for people with a rare inherited eye disease that causes blindness. 30 participants aged 6 and older were randomly assigned to receive the therapy or no treatment. The goal is to see if the treatment improves functional vision and light sensitivity.

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Contacts and locations

Locations

  • Shanghai General Hospital

    Shanghai, China

  • Southwest Hospital of AMU

    Chongqing, China

  • Tianjin Medical University Ophthalmology Hospital

    Tianjin, China

  • Zhongshan Ophthalmic Center, Sun Yat sen University

    Guangzhou, Guangdong, China

Conditions

Explore the condition pages connected to this study.