Five-Year watch on Vision-Saving gene therapy
NCT ID NCT04312672
Summary
This study followed 42 adults and children for up to 5 years after they received an experimental gene therapy for a genetic eye disease called X-linked retinitis pigmentosa. The main goal was to check for any long-term safety issues from the treatment. Researchers also tracked whether participants' vision, like their ability to see in dim light or navigate a course, changed over time.
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Contacts and locations
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Locations
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Leeds Teaching Hospitals NHS Trust
Leeds, LS9 7TF, United Kingdom
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Massachusetts Eye and Ear Infirmary
Boston, Massachusetts, 02114, United States
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Moorfields Eye Hospital
London, EC1V 9EL, United Kingdom
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Univ of Michigan Medical Center
Ann Arbor, Michigan, 48105, United States
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University of Pittsburgh Medical Center
Pittsburgh, Pennsylvania, 15213, United States
Conditions
Explore the condition pages connected to this study.