Experimental gene therapy for rare muscle disease halted early
NCT ID NCT05906251
First seen Nov 01, 2025 · Last updated Apr 24, 2026 · Updated 21 times
Summary
This study tested a gene therapy called SRP-6004 for people with limb girdle muscular dystrophy type 2B/R2, a rare muscle-weakening disease. The goal was to check if the treatment was safe and could help muscles work better. Only 2 people took part before the study was stopped early.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
Conditions
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