Gene therapy breakthrough trial opens for hemophilia patients previously ineligible
NCT ID NCT06003387
Summary
This study is testing a one-time gene therapy called CSL222 in adults with severe hemophilia B who have pre-existing antibodies that normally block this type of treatment. The main goal is to see if the therapy safely reduces bleeding episodes and the need for regular clotting factor injections. Researchers will enroll about 35 participants to measure bleeding rates, safety, and quality of life over time.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Centro de Investigacion Clinica GRAMEL S.C.
RECRUITINGMexico City, Mexico City, 3720, Mexico
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Changhua Christian Hospital (CCH)
RECRUITINGChang-hua, 500, Taiwan
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Ege University Medical Faculty
RECRUITINGBornova, 35100, Turkey (Türkiye)
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Gaziantep University Sahinbey Research and Practice Hospital
RECRUITINGGaziantep, 27310, Turkey (Türkiye)
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Haemophilia Comprehensive Care Centre
RECRUITINGJohannesburg, 2193, South Africa
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Kaohsiung Medical University Chung-Ho Memorial Hospital (KMUH)
RECRUITINGKaohsiung City, Sanmin District, 80756, Taiwan
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King Faisal Specialist Hospital and Research Center
RECRUITINGRiyadh, 11471, Saudi Arabia
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Kyung Hee University Hospital at Gangdong
RECRUITINGSeoul, 05278, South Korea
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Kyungpook National University Hospital
RECRUITINGDaegu, 41944, South Korea
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McMaster University - Hamilton
RECRUITINGHamilton, Ontario, L8N 3Z5, Canada
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National Taiwan University Hospital
RECRUITINGTaipei, 100225, Taiwan
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National University Hospital
RECRUITINGSingapore, 110974, Singapore
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Prince of Wales Hospital Chinese University of Hong Kong
RECRUITINGShatin, 999077, Hong Kong
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Queen Mary Hospital
RECRUITINGHong Kong, 999077, Hong Kong
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Royal Adelaide Hospital
RECRUITINGAdelaide, South Australia, 5000, Australia
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Royal Brisbane Hospital
RECRUITINGHerston, Queensland, 4029, Australia
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Royal Prince Alfred Hospital
RECRUITINGCamperdown, New South Wales, 2050, Australia
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Severance Hospital, Yonsei University Health System
RECRUITINGSeoul, 3722, South Korea
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Sheba Medical Center
RECRUITINGTel Litwinsky, 5265601, Israel
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Singapore General Hospital
RECRUITINGSingapore, 169608, Singapore
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Taichung Veterans General Hospital -
RECRUITINGTaichung, 40705, Taiwan
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The Alfred Hospital
RECRUITINGMelbourne, Victoria, 3004, Australia
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Tri-Service General Hospital
RECRUITINGTaipei, Neihu District, 114, Taiwan
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University of California, San Diego (UCSD)
RECRUITINGSan Diego, California, 92121, United States
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University of Michigan
RECRUITINGAnn Arbor, Michigan, 48109, United States
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Özel Acibadem Adana Hastanesi
RECRUITINGSeyhan, 01130, Turkey (Türkiye)
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Conditions
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