Gene therapy breakthrough trial opens for hemophilia patients previously ineligible

NCT ID NCT06003387

Summary

This study is testing a one-time gene therapy called CSL222 in adults with severe hemophilia B who have pre-existing antibodies that normally block this type of treatment. The main goal is to see if the therapy safely reduces bleeding episodes and the need for regular clotting factor injections. Researchers will enroll about 35 participants to measure bleeding rates, safety, and quality of life over time.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Centro de Investigacion Clinica GRAMEL S.C.

    RECRUITING

    Mexico City, Mexico City, 3720, Mexico

    Contact

  • Changhua Christian Hospital (CCH)

    RECRUITING

    Chang-hua, 500, Taiwan

    Contact

  • Ege University Medical Faculty

    RECRUITING

    Bornova, 35100, Turkey (Türkiye)

    Contact

  • Gaziantep University Sahinbey Research and Practice Hospital

    RECRUITING

    Gaziantep, 27310, Turkey (Türkiye)

    Contact

  • Haemophilia Comprehensive Care Centre

    RECRUITING

    Johannesburg, 2193, South Africa

    Contact

  • Kaohsiung Medical University Chung-Ho Memorial Hospital (KMUH)

    RECRUITING

    Kaohsiung City, Sanmin District, 80756, Taiwan

    Contact

  • King Faisal Specialist Hospital and Research Center

    RECRUITING

    Riyadh, 11471, Saudi Arabia

    Contact

  • Kyung Hee University Hospital at Gangdong

    RECRUITING

    Seoul, 05278, South Korea

    Contact

  • Kyungpook National University Hospital

    RECRUITING

    Daegu, 41944, South Korea

    Contact

  • McMaster University - Hamilton

    RECRUITING

    Hamilton, Ontario, L8N 3Z5, Canada

    Contact

  • National Taiwan University Hospital

    RECRUITING

    Taipei, 100225, Taiwan

  • National University Hospital

    RECRUITING

    Singapore, 110974, Singapore

    Contact

  • Prince of Wales Hospital Chinese University of Hong Kong

    RECRUITING

    Shatin, 999077, Hong Kong

    Contact

  • Queen Mary Hospital

    RECRUITING

    Hong Kong, 999077, Hong Kong

    Contact

  • Royal Adelaide Hospital

    RECRUITING

    Adelaide, South Australia, 5000, Australia

  • Royal Brisbane Hospital

    RECRUITING

    Herston, Queensland, 4029, Australia

    Contact

  • Royal Prince Alfred Hospital

    RECRUITING

    Camperdown, New South Wales, 2050, Australia

    Contact

  • Severance Hospital, Yonsei University Health System

    RECRUITING

    Seoul, 3722, South Korea

    Contact

  • Sheba Medical Center

    RECRUITING

    Tel Litwinsky, 5265601, Israel

    Contact

  • Singapore General Hospital

    RECRUITING

    Singapore, 169608, Singapore

  • Taichung Veterans General Hospital -

    RECRUITING

    Taichung, 40705, Taiwan

    Contact

  • The Alfred Hospital

    RECRUITING

    Melbourne, Victoria, 3004, Australia

    Contact

  • Tri-Service General Hospital

    RECRUITING

    Taipei, Neihu District, 114, Taiwan

    Contact

  • University of California, San Diego (UCSD)

    RECRUITING

    San Diego, California, 92121, United States

    Contact

  • University of Michigan

    RECRUITING

    Ann Arbor, Michigan, 48109, United States

    Contact

  • Özel Acibadem Adana Hastanesi

    RECRUITING

    Seyhan, 01130, Turkey (Türkiye)

    Contact

Conditions

Explore the condition pages connected to this study.