Gene therapy could help hemophilia b patients stop bleeding
NCT ID NCT03961243
First seen Apr 24, 2026 · Last updated Apr 24, 2026
Summary
This early-stage trial tests a gene therapy for hemophilia B, a bleeding disorder. Doctors take a patient's own stem cells, add a working gene for clotting factor IX, and put them back. The goal is to see if it's safe and helps the body make its own clotting factor, reducing the need for regular factor infusions. The study involves 10 males aged 2 and older with severe hemophilia B.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Shenzhen Geno-immune Medical Institute
RECRUITINGShenzhen, Guangdong, 518000, China
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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