New gene therapy could help hemophilia b patients stop bleeding
NCT ID NCT03961243
First seen Apr 24, 2026 · Last updated Jun 13, 2026 · Updated 6 times
Summary
This early-stage study tests a gene therapy for hemophilia B, a bleeding disorder. Ten male participants (age 2 and up) will receive their own stem cells modified with a lentiviral vector to produce clotting factor IX. The goal is to see if the treatment is safe and can reduce bleeding episodes. Because the therapy aims to provide long-term factor IX production but does not eliminate the need for monitoring or potential future treatment, it is classified as disease control.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Shenzhen Geno-immune Medical Institute
RECRUITINGShenzhen, Guangdong, 518000, China
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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