New gene therapy trial hopes to slow duchenne muscular dystrophy
NCT ID NCT04626674
First seen Jan 04, 2026 · Last updated May 05, 2026 · Updated 21 times
Summary
This study tests a gene therapy called delandistrogene moxeparvovec in 83 people with Duchenne muscular dystrophy (DMD). The goal is to see if it is safe and helps the body produce a key muscle protein. Participants include both children and adults who can walk or use a wheelchair, and the study lasts up to 156 weeks.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Arkansas Children's Hospital
RECRUITINGLittle Rock, Arkansas, 72202, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Children's Hospital of The King's Daughters
RECRUITINGNorfolk, Virginia, 23507, United States
Contact Email: •••••@•••••
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Nationwide Children's Hospital
ACTIVE_NOT_RECRUITINGColumbus, Ohio, 43205, United States
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Neurology Rare Disease Center
RECRUITINGFlower Mound, Texas, 75028, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Stanford University
RECRUITINGPalo Alto, California, 94304, United States
Contact Email: •••••@•••••
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University of California, Davis
RECRUITINGSacramento, California, 95616, United States
Contact
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Washington University in St. Louis
RECRUITINGSt Louis, Missouri, 63110, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Conditions
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