Researchers ask families: what do you need to know about gene therapy?

NCT ID NCT05810181

Summary

This study aims to understand what patients and families think and need to know when considering gene therapy for rare diseases like sickle cell. Researchers will interview patients, parents, and healthcare workers about their experiences and concerns. Using what they learn, the team will create an online platform with educational materials and tools to help families make informed treatment decisions.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for SICKLE CELL DISEASE are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • St. Jude Children's Research Hospital

    RECRUITING

    Memphis, Tennessee, 38105, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.