One-Shot gene fix tested for devastating fat disease

NCT ID NCT07176923

Summary

This is a very early safety study for a new, one-time gene-editing treatment called CS-121. It aims to help adults with a rare, inherited condition where the body cannot properly clear fat from the blood, leading to dangerously high levels and painful, life-threatening pancreas attacks. Researchers will give a single infusion to a small group of patients to see if it is safe and if it lowers their blood fat levels.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • The First Affiliated Hospital of Anhui Medical University

    RECRUITING

    Hefei, Anhui, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

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