New antibody shows promise for rare muscle disease

NCT ID NCT05548556

First seen Nov 01, 2025 · Last updated Apr 28, 2026 · Updated 17 times

Summary

This study tests an experimental drug called RO7204239 in 51 adults with facioscapulohumeral muscular dystrophy (FSHD), a genetic condition that causes progressive muscle weakness. The drug is designed to block a protein that limits muscle growth, aiming to slow muscle loss. Participants receive either the drug or a placebo, and researchers measure changes in muscle volume and safety over time.

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Contacts and locations

Locations

  • Asst Grande Ospedale Metropolitano Niguarda

    Milan, Lombardy, 20162, Italy

  • Kennedy Krieger Institute

    Baltimore, Maryland, 21205, United States

  • National Hospital for Neurology and Neurosurgery,

    London, WC1N 3BG, United Kingdom

  • Policlinico Universitario Agostino Gemelli

    Rome, Lazio, 00168, Italy

  • Regents of the University of Colorado

    Aurora, Colorado, 80045, United States

  • Rigshospitalet

    København Ø, 2100, Denmark

  • Royal Victoria Infirmary

    Newcastle upon Tyne, NE1 4LP, United Kingdom

  • University of Irvine Medical Center (UCIMC)

    Orange, California, 92868, United States

  • University of Kansas Medical Center

    Fairway, Kansas, 66205, United States

  • Virginia Commonwealth University Medical Center

    Richmond, Virginia, 23298-0599, United States

Conditions

Explore the condition pages connected to this study.