New drug aims to build muscle, fight rare genetic disease

NCT ID NCT05548556

Summary

This study is testing an investigational drug called RO7204239 to see if it can increase muscle volume and slow disease progression in adults with FSHD, a genetic muscle-wasting disorder. The trial will measure changes in muscle size using MRI scans and check the drug's safety. Participants are adults with FSHD who can walk without assistance.

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Contacts and locations

Locations

  • Asst Grande Ospedale Metropolitano Niguarda

    Milan, Lombardy, 20162, Italy

  • Kennedy Krieger Institute

    Baltimore, Maryland, 21205, United States

  • National Hospital for Neurology and Neurosurgery,

    London, WC1N 3BG, United Kingdom

  • Policlinico Universitario Agostino Gemelli

    Rome, Lazio, 00168, Italy

  • Regents of the University of Colorado

    Aurora, Colorado, 80045, United States

  • Rigshospitalet

    København Ø, 2100, Denmark

  • Royal Victoria Infirmary

    Newcastle upon Tyne, NE1 4LP, United Kingdom

  • University of Irvine Medical Center (UCIMC)

    Orange, California, 92868, United States

  • University of Kansas Medical Center

    Fairway, Kansas, 66205, United States

  • Virginia Commonwealth University Medical Center

    Richmond, Virginia, 23298-0599, United States

Conditions

Explore the condition pages connected to this study.