Gene therapy shows promise for rare 'Butterfly Skin' wounds
NCT ID NCT04213261
First seen Mar 23, 2026 · Last updated May 12, 2026 · Updated 5 times
Summary
This study tests a gene therapy called FCX-007 for people with recessive dystrophic epidermolysis bullosa (RDEB), a rare skin condition causing severe blistering. The treatment uses the patient's own skin cells, modified to produce a missing protein, and is injected into wounds. The goal is to see if it helps wounds close better than standard care alone. The study involves 6 participants aged 2 and older.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Children's Hospital Colorado
Aurora, Colorado, 80045, United States
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Dell Children's Medical Group
Austin, Texas, 78723, United States
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Mayo Clinic
Rochester, Minnesota, 55905, United States
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Solutions Through Advanced Research, Inc.
Jacksonville, Florida, 32256, United States
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Stanford University
Stanford, California, 94305, United States
Conditions
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