Experimental injection aims to tackle root cause of rare liver disease

NCT ID NCT03946449

Summary

This small, early-stage study tested an investigational drug called fazirsiran in people with liver disease caused by Alpha-1 antitrypsin deficiency. Sixteen participants received multiple injections under the skin to see if the drug could safely reduce the harmful protein that builds up in the liver. Researchers measured changes in liver protein levels, scarring, and inflammation over 24 to 48 weeks.

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Contacts and locations

Locations

  • Research Center 1

    Vienna, 1090, Austria

  • Research Center 1

    Aachen, 52074, Germany

  • Research Center 2

    Edinburgh, EH19 3BJ, United Kingdom

  • Research Center 3

    Cambridge, CB2 0QQ, United Kingdom

Conditions

Explore the condition pages connected to this study.