Researchers test speeding up lifelong treatment for rare disease
NCT ID NCT06019728
Summary
This study aimed to see if the approved drug Fabrazyme, used to manage Fabry disease, could be safely infused at a faster rate. It involved 8 participants already stable on the treatment to test if shortening infusion times was tolerable. The goal was to reduce the treatment time burden for people who need these lifelong infusions.
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Contacts and locations
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Locations
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Emory University School of Medicine Site Number : 1005
Atlanta, Georgia, 30322-1007, United States
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Infusion Associates Site Number : 1001
Grand Rapids, Michigan, 49525, United States
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Lysosomal and Rare Disorders Research and Treatment Center, Inc Site Number : 1002
Fairfax, Virginia, 22030, United States
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Metropolitan Hospital Center Site Number : 1004
New York, New York, 10021, United States
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UCLA Medical Center Site Number : 1003
Santa Monica, California, 90404, United States
Conditions
Explore the condition pages connected to this study.