New hope for rare disease patients in china

NCT ID NCT05054387

Summary

This study tested the safety and effectiveness of Fabrazyme, an enzyme replacement therapy, for Chinese patients with Fabry disease. Twenty-two participants received treatment for 48 weeks while researchers monitored side effects and changes in disease markers. The goal was to understand how well this established treatment works specifically in the Chinese population.

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Contacts and locations

Locations

  • Investigational Site Number :1560001

    Shanghai, 200025, China

  • Investigational Site Number :1560002

    Beijing, 100730, China

  • Investigational Site Number :1560003

    Beijing, 100034, China

  • Investigational Site Number :1560004

    Shanghai, 201102, China

  • Investigational Site Number :1560005

    Wuhan, 016040, China

  • Investigational Site Number :1560006

    Taiyuan, 030001, China

Conditions

Explore the condition pages connected to this study.