New hope for fabry patients: experimental drug enters human trials
NCT ID NCT06858397
First seen Nov 01, 2025 · Last updated May 09, 2026 · Updated 26 times
Summary
This early-stage study tests a new medicine called HM15421 in 18 adults with Fabry disease, a rare genetic condition that causes pain, organ damage, and other serious problems. The main goal is to see if the drug is safe and to find the right dose. Researchers will also check if it helps control the disease by measuring drug levels in the blood and watching for side effects.
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This is a summary of
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Centro Medico IPAM
RECRUITINGRosario, Santa Fe Province, S2000, Argentina
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Children's Hospital Medical Center
RECRUITINGCincinnati, Ohio, 45229-3039, United States
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David Geffen School of Medicine UCLA, UCLA Health
RECRUITINGLos Angeles, California, 90095, United States
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Hospital Italiano de Buenos Aires
RECRUITINGBuenos Aires, C1199ABB, Argentina
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Lysosomal and Rare Disorders Research and Treatment Center
RECRUITINGFairfax, Virginia, 22030, United States
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Pusan National University Children's Hospital in Yangsan
RECRUITINGYangsan, Gyeongsangnam-do, 50612, South Korea
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University of Kansas School of Medicine
RECRUITINGKansas City, Kansas, 66160-8500, United States
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University of Minnesota
RECRUITINGMinneapolis, Minnesota, 55455, United States
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University of Pittsburgh Medical Center Children's Hoispital of Pittsburgh
RECRUITINGPittsburgh, Pennsylvania, 15224, United States
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Yonsei University, College of Medicine
RECRUITINGSeoul, 03722, South Korea
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Conditions
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