New hope for japanese families battling rare genetic disease
NCT ID NCT05710692
Summary
This study is testing a new drug called pegunigalsidase alfa (PRX-102) for Japanese adults and teenagers with Fabry disease, a rare genetic disorder. The main goal is to see if the drug is safe and if it can help prevent or reduce the health problems caused by the disease. Participants will receive the drug through an IV every two or four weeks for at least a year.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Asahikawa Medical University Hospital
RECRUITINGAsahikawa, Japan
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Fukuoka University Chikushi Hospital
WITHDRAWNChikushino-shi, Fukuoka, 818-8502, Japan
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Juntendo University Hospital, 3-1-3 Hongo, Bunkyo-ku, Tokyo
RECRUITINGBunkyo-ku, Tokyo, 113-0033, Japan
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Keio University Hospital
RECRUITINGShinjuku-ku, Tokyo, 160-8582, Japan
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Niigata University Medical & Dental Hospital
RECRUITINGNiigata, 951-8520, Japan
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Osaka University Hospital
RECRUITINGSuita, Osaka, 565-0871, Japan
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Tohoku University Hospital
RECRUITINGSendai, Miyagi, 980-8574, Japan
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Tokyo Jikei University Hospital
RECRUITINGMinato-ku, Tokyo, 105-8461, Japan
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University of the Ryukyu Hospital
RECRUITINGNishihara, Okinawa, 903-0125, Japan
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Conditions
Explore the condition pages connected to this study.