Eye injection may save sight in kids with rare batten disease
NCT ID NCT05152914
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tests whether injecting a replacement enzyme directly into the eye can slow or stop vision loss in children with CLN2 Batten disease, a rare genetic disorder that causes blindness and brain damage. Five children aged 2 to 6 who already receive brain infusions of the enzyme will get eye injections over two years. The goal is to see if the treatment is safe and helps preserve retinal structure and eyesight.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
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The condition terms exactly as the trial's registrant entered them.
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Locations
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States