Experimental treatment offered to patients with rare metabolic disorder

NCT ID NCT03773770

Summary

This program provides access to an experimental medication called triheptanoin for patients with Long Chain Fatty Acid Oxidation Disorders (LC-FAOD). It's for patients who have limited treatment options and cannot participate in clinical trials. The goal is to help manage this rare metabolic condition by providing an alternative energy source for the body.

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Contacts and locations

Study contacts

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    Phone: •••-•••-•••• Email: •••••@•••••

Conditions

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