New registry aims to map rare genetic diseases that harden arteries in babies

NCT ID NCT06302439

First seen Dec 30, 2025 · Last updated May 16, 2026 · Updated 15 times

Summary

This study is a patient registry that will follow up to 1,000 people with ENPP1 deficiency or infantile-onset ABCC6 deficiency. Researchers will collect information from routine doctor visits, including genetic, imaging, and quality-of-life data, to better understand how these rare diseases progress. The goal is to learn about the full burden of illness, not to test a new treatment.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Ann and Robert H. Lurie Children's Hospital

    RECRUITING

    Chicago, Illinois, 60611, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • CHU Sainte-Justine Research Centre

    RECRUITING

    Montreal, Quebec, H3T1C5, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • CLINILABS Drug Development Corp

    RECRUITING

    Eatontown, New Jersey, 07724, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • EU Hub - VCTC

    RECRUITING

    Barcelona, 08029, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hospital Sant Joan de Deu

    RECRUITING

    Barcelona, 08950, Spain

    Contact Phone: •••-•••-••••

    Contact

  • IRCCS San Raffaele Hospital - Main

    RECRUITING

    Milan, 20132, Italy

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Mayo Clinic

    RECRUITING

    Rochester, Minnesota, 55905, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Royal Hospital Muscat

    RECRUITING

    Muscat, Oman

    Contact

  • The Children's Hospital of Philadelphia (CHOP)

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The University of Tokyo Hospital

    RECRUITING

    Tokyo, 113-8655, Japan

    Contact

  • Umraniye Training and Research Hospital

    RECRUITING

    Istanbul, 34764, Turkey (Türkiye)

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Universitätsklinikum Hamburg-Eppendorf

    RECRUITING

    Hamburg, 20251, Germany

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • VCTC

    RECRUITING

    Derby, DE11 7AQ, United Kingdom

    Contact Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.