New study aims to prevent liver damage from duchenne gene therapy
NCT ID NCT07542314
First seen Apr 22, 2026 · Last updated May 23, 2026 · Updated 7 times
Summary
This study tests whether adding the drug sirolimus can reduce the risk of acute liver injury in people with Duchenne muscular dystrophy who receive the gene therapy ELEVIDYS. About 20 participants will be enrolled to monitor safety and side effects. The goal is to make this treatment safer for long-term disease control.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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