New hope for babies with hemophilia: once-every-2-weeks shot cuts bleeding risk
NCT ID NCT04431726
First seen Nov 01, 2025 · Last updated May 15, 2026 · Updated 26 times
Summary
This study tests a medicine called emicizumab in 55 babies from birth to 12 months old with severe hemophilia A. The medicine is given as a shot under the skin every 2 weeks for a year, then less often for up to 7 more years. The goal is to see if it safely reduces the number of bleeding episodes. This is a long-term treatment, not a cure.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for SEVERE HEMOPHILIA A are added.
By submitting, you agree to our Terms of use
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Locations
-
AORN Santobono Pausilipon
Naples, Campania, 80123, Italy
-
AOU Careggi
Florence, Tuscany, 50134, Italy
-
AOU di Parma
Parma, Emilia-Romagna, 43126, Italy
-
Adana Acibadem Hospital
Adana, 01130, Turkey (Türkiye)
-
Charlotte Maxeke Johannesburg Hospital
Johannesburg, 2193, South Africa
-
Children's Hospital Los Angeles
Los Angeles, California, 90027, United States
-
Children's Hospital of Eastern Ontario
Ottawa, Ontario, K1H 8L1, Canada
-
Cliniques Universitaires St-Luc
Brussels, 1200, Belgium
-
Ege University, School of Medicine
Izmir, 35100, Turkey (Türkiye)
-
Groupe Hospitalier Necker Enfants Malades
Paris, 75015, France
-
Hacettepe University Medical Faculty
Ankara, 06100, Turkey (Türkiye)
-
Hospital Sant Joan de Deu
Esplugues de Llobregat, Barcelona, 08950, Spain
-
Hospital Universitario Virgen del Rocio
Seville, 41013, Spain
-
Hospital Universitario la Paz
Madrid, 28046, Spain
-
Hospital das Clínicas Faculdades Médicas de Ribeirão Preto
Ribeirão Preto, São Paulo, 14051-140, Brazil
-
Hämophilie-Zentrum Rhein Main GmbH
Mörfelden-Walldorf, 64546, Germany
-
IRCCS Ca' Granda Ospedale Maggiore Policlinico
Milan, Lombardy, 20122, Italy
-
Medizinische Universität Wien
Vienna, 1090, Austria
-
Ondokuz Mayis Univ. Med. Fac.
Samsun, 55139, Turkey (Türkiye)
-
Perth Children's Hospital
Nedlands, Western Australia, 6009, Australia
-
Phoenix Children's Hospital
Phoenix, Arizona, 85016, United States
-
Queen Elizabeth University Hospital
Glasgow, G51 4TF, United Kingdom
-
Royal Children's Hospital
Parkville, Victoria, 3052, Australia
-
Seattle Children's Hospital
Seattle, Washington, 98105, United States
-
Sheba Medical Center - National Hemophilia Center
Tel Litwinsky, 5262100, Israel
-
The Children's Hospital at Westmead
Westmead, New South Wales, 2145, Australia
-
The Hospital for Sick Children
Toronto, Ontario, M5G 1X8, Canada
-
Tulane University Health Sciences Center
New Orleans, Louisiana, 70112, United States
-
UZ Leuven Gasthuisberg
Leuven, 3000, Belgium
-
University of Colorado Denver, Children's Hospital
Aurora, Colorado, 80045, United States
-
University of Michigan
Ann Arbor, Michigan, 48109-0934, United States
-
Universitätsklinikum Bonn
Bonn, 53127, Germany
Conditions
Explore the condition pages connected to this study.