New drug trial aims to control debilitating muscle disease
NCT ID NCT06298552
Summary
This study is testing whether an intravenous drug called efgartigimod is effective and safe for adults with a specific, hard-to-treat form of generalized myasthenia Gravis (gMG). About 119 participants will be randomly assigned to receive either the drug or a placebo for part of the study, followed by an open-label period where all receive the drug. The main goal is to see if the treatment improves patients' daily activities and muscle strength over approximately 2.5 years.
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Contacts and locations
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Locations
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AHEPA University General Hospital of Thessaloniki
Thessaloniki, 546 36, Greece
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AP-HM- Hôpital de La Timone
Marseille, 13386, France
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AP-HP - Hôpital de la Pitié Salpétrière
Paris, 75013, France
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AZ Sint-Lucas Gent
Ghent, 9000, Belgium
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Aarhus Universitetshospital
Aarhus, 8200, Denmark
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BayCare - St. Anthony's Hospital
St. Petersburg, Florida, 33705-1410, United States
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CHU de Nice-Hôpital Pasteur
Nice, 06000, France
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CLINIREM Sp z o.o.
Lublin, 20-883, Poland
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Centrum Medyczne Neurologia Slaska
Katowice, 40-689, Poland
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Charité - Universitätsmedizin Berlin
Berlin, 13353, Germany
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Cleveland Clinic
Cleveland, Ohio, 44195, United States
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Cliniques Universitaires Saint-Luc
Brussels, 1200, Belgium
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Cluj County Emergency Clinical Hospital
Cluj-Napoca, 400012, Romania
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Cyprus Institute of Neurology and Genetics
Égkomi, 2371, Cyprus
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Desai Sethi Medical Center
Miami, Florida, 33136, United States
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Duke University School of Medicine - Duke Early Phase Clinical Research Unit
Durham, North Carolina, 27710, United States
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Eginitio Hospital
Athens, 115 28, Greece
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Erlanger Neuroscience Institute
Chattanooga, Tennessee, 37403-2173, United States
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Fakultni nemocnice Brno
Brno, 625 00, Czechia
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First Choice Neurology Boca Raton
Boca Raton, Florida, 33428, United States
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First Hospital of Shanxi Medical University
Taiyuan, 030001, China
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Fujian Medical University Union Hospital
Fuzhou, 350001, China
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Genge Partners Inc.
Montreal, H4A 3T2, Canada
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Guangdong Province Traditional Chinese Medical Hospital
Guangzhou, 518053, China
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Haukeland Universitetssykehus
Bergen, 5021, Norway
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Heritage Medical Research Clinic
Calgary, T2N 4Z6, Canada
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HonorHealth Neurology - Bob Bove Neuroscience Institute
Scottsdale, Arizona, 85251, United States
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Hospital Clinico Universitario de Santiago
Santiago de Compostela, 15706, Spain
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Hospital General Universitario Dr. Balmis
Alicante, 03010, Spain
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Hospital Universitari Arnau de Vilanova
Lleida, 25198, Spain
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Hospital Universitari i Politecnic La Fe de Valencia
Valencia, 46026, Spain
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Hospital Universitario Ramon y Cajal
Madrid, 28304, Spain
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Hospital Universitario Vall d'Hebron - PPDS
Barcelona, 8035, Spain
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Hospital de La Santa Creu i Sant Pau
Barcelona, 8041, Spain
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Hospital de Santo António - Unidade Local de Saúde de Santo António
Porto, 4050-011, Portugal
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Huashan Hospital Fudan University
Shanghai, 200040, China
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Hôpital Erasme
Anderlecht, 1070, Belgium
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Kansas University Medical Center - Kansas City
Fairway, Kansas, 66205, United States
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Katholisches Klinikum Bochum - St. Josef Hospital
Bochum, 44791, Germany
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King Faisal Specialist Hospital & Research Center
Riyadh, 11211, Saudi Arabia
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Krakowska Akademia Neurologii Sp. z o.o.
Krakow, 31-505, Poland
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LLC Caucasus Medical Centre
Tbilisi, 0186, Georgia
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Leeds General Infirmary
Leeds, LS1 3EX, United Kingdom
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Leiden University Medical Center
Leiden, 2333 ZA, Netherlands
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Loma Linda University Health
Fresno, California, 93701-2234, United States
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MICS Centrum Medyczne Bydgoszcz
Bydgoszcz, 85-065, Poland
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Medsol Clinical Research Center Inc
Port Charlotte, Florida, 33952, United States
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National Guard Riyadh
Riyadh, 14611, Saudi Arabia
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National Neuromuscular Research Institute
Austin, Texas, 78756, United States
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Nemocnice Pardubickeho kraje, a.s., Pardubicka nemocnice
Pardubice, 530 03, Czechia
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Neurology Associates PA
Maitland, Florida, 32751, United States
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New Hospitals
Tbilisi, 0114, Georgia
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Ningbo Medical Center Lihuili Hospital
Ningbo, 315041, China
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Odense Universitetshospital
Odense C, 5000, Denmark
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Opsta bolnica MSB - Medicinski Sistemi Beograd
Belgrade, 11000, Serbia
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Oslo Universitetssykehus HF, Ullevål
Oslo, 424, Norway
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Ottawa Hospital - Civic Campus
Ottawa, K1H 8L6, Canada
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Panthera Biopartners
Glasgow, G51 4TY, United Kingdom
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Petre Sarajishvili Institute of Neurology
Tbilisi, 0112, Georgia
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Pineo Medical Ecosystem
Tbilisi, 0112, Georgia
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Qilu Hospital of Shandong University
Qingdao, 266035, China
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Rigshospitalet
Copenhagen, 2100, Denmark
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Rutgers-Robert Wood Johnson Medical School
New Brunswick, New Jersey, 08901-1962, United States
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SFM Clinical Research LLC
Boca Raton, Florida, 33487, United States
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Semmelweis Egyetem Genomikai Medicina és Ritka Betegségek Intézete
Budapest, 1082, Hungary
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Sibiu Emergency County Clinical Hospital
Sibiu, 550166, Romania
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Sichuan Academy of Medical Sciences & Sichuan Provincial People's Hospital
Chongqing, 400016, China
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Szpital Uniwersytecki w Krakowie
Krakow, 31-503, Poland
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The Affiliated Hospital of Guizhou Medical University
Guiyang, 550004, China
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The First Affiliated Hospital of Chongqing Medical University
Chongqing, 400016, China
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The First Affiliated Hospital of Guangxi Medical University
Guangxi, 530021, China
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The First Affiliated Hospital of Guangzhou University Chinese Medicine
Guangzhou, 510405, China
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The First Hospital of Jilin University
Changchun, 130021, China
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The Neurology Institute / Healthcare Innovations Institute - Coral Springs
Coral Springs, Florida, 33067, United States
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Tongji Hospital Tongji Medical College Huazhong University of Science and Technology
Wuhan, 430030, China
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Turun Yliopistollinen Keskussairaala
Turku, 20540, Finland
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ULS de Lisboa Ocidental, EPE - Hospital Egas Moniz
Lisbon, 1349-019, Portugal
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ULS de Santa Maria, EPE - Hospital de Santa Maria
Lisbon, 1150-199, Portugal
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UZ Leuven
Leuven, 3000, Belgium
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Universitair Medisch Centrum Utrecht
Utrecht, 3584 CX, Netherlands
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University Clinical Center Kragujevac
Kragujevac, 34000, Serbia
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University General Hospital ''ATTIKON''
Chaïdári, 124 62, Greece
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University General Hospital of Patras
Pátrai, 265 04, Greece
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University of North Carolina - Chapel Hill
Chapel Hill, North Carolina, 27599-7025, United States
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University of South Florida (USF) Health - Morsani Center for Advanced Healthcare
Tampa, Florida, 33612, United States
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University of Washington Medical Center - Montlake
Seattle, Washington, 98195, United States
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Universitätsklinikum Würzburg
Würzburg, 97080, Germany
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Uniwersytecki Szpital Kliniczny im. Jana Mikulicza Radeckiego we Wroclawiu
Wroclaw, 50-556, Poland
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Wellstar - Augusta University Medical Center
Augusta, Georgia, 30912, United States
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West Georgia Medical Center
Kutaisi, 4600, Georgia
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Xuanwu Hospital Capital Medical University
Beijing, 100053, China
Conditions
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