Promising drug for kids with rare muscle disease enters final testing phase

NCT ID NCT06392386

Recruiting now Disease control Sponsor: argenx Source: ClinicalTrials.gov ↗

First seen Jan 06, 2026 · Last updated May 13, 2026 · Updated 19 times

Summary

This study tests a drug called efgartigimod in children aged 2 to 17 with generalized myasthenia gravis, a condition that causes muscle weakness. The goal is to find the right dose and check for side effects. Participants receive injections and are monitored for up to 14 weeks.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

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Study contacts

Contact

Phone: •••-•••-•••• Email: •••••@•••••

Locations

AP-HM- Hôpital de La Timone
RECRUITING

Marseille, 13385, France

Contact Phone: •••-•••-•••• Email: •••••@•••••
Carolinas HealthCare System Neurosciences Institute - Neurology
RECRUITING

Charlotte, North Carolina, 28207, United States

Contact Phone: •••-•••-•••• Email: •••••@•••••
Centralny Szpital Kliniczny - Uniwersyteckie Centrum Kliniczne WUM
RECRUITING

Warsaw, 02-097, Poland

Contact Phone: •••-•••-•••• Email: •••••@•••••
Childrens Hospital of Eastern Ontario
RECRUITING

Ottawa, K1H 8L1, Canada

Contact Phone: •••-•••-•••• Email: •••••@•••••
Fakultni nemocnice Brno
RECRUITING

Brno, 613 00, Czechia

Contact Phone: •••-•••-•••• Email: •••••@•••••
Fakultni nemocnice Ostrava
RECRUITING

Ostrava, 708 00, Czechia

Contact Phone: •••-•••-•••• Email: •••••@•••••
Hadassah Medical Center- Ein Kerem
RECRUITING

Jerusalem, 9112001, Israel

Contact Phone: •••-•••-•••• Email: •••••@•••••
Hospital Universitari i Politecnic La Fe de Valencia
RECRUITING

Valencia, 46026, Spain

Contact Phone: •••-•••-•••• Email: •••••@•••••
Hôpital Nestlé
RECRUITING

Lausanne, 1011, Switzerland

Contact Phone: •••-•••-•••• Email: •••••@•••••
Istituto G Gaslini Ospedale Pediatrico IRCCS
RECRUITING

Genova, 16147, Italy

Contact Phone: •••-•••-•••• Email: •••••@•••••
Leiden University Medical Center
RECRUITING

Leiden, 2333 ZA, Netherlands

Contact Phone: •••-•••-•••• Email: •••••@•••••
Neurologia Śląska Centrum Medyczne
RECRUITING

Katowice, 40-689, Poland

Contact Phone: •••-•••-•••• Email: •••••@•••••
Neurology Rare Disease Center
RECRUITING

Denton, Texas, 76208, United States

Contact Phone: •••-•••-•••• Email: •••••@•••••
Oxford Children's Hospital
RECRUITING

Oxford, OX3 9DU, United Kingdom

Contact Phone: •••-•••-•••• Email: •••••@•••••
Schneider Children's Medical Center of Israel
RECRUITING

Petah Tikvah, 4920235, Israel

Contact Phone: •••-•••-•••• Email: •••••@•••••
Tel Aviv Sourasky Medical Center Ichilov
RECRUITING

Tel Aviv, 6423906, Israel

Contact Phone: •••-•••-•••• Email: •••••@•••••
UZ Gent
RECRUITING

Ghent, 9000, Belgium

Contact Phone: •••-•••-•••• Email: •••••@•••••
University of Virginia
RECRUITING

Charlottesville, Virginia, 22903, United States

Contact Phone: •••-•••-•••• Email: •••••@•••••
Universitätsklinikum Essen
RECRUITING

Essen, 45147, Germany

Contact Phone: •••-•••-•••• Email: •••••@•••••
Uniwersyteckie Centrum Kliniczne w Gdansku
RECRUITING

Gdansk, 80-211, Poland

Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.

GENERALIZED MYASTHENIA GRAVIS