New drug trial aims to protect kids from rare swelling disorder

NCT ID NCT07298447

Summary

This study is testing a drug called donidalorsen in children aged 2 to 12 who have hereditary angioedema (HAE), a rare condition that causes sudden, severe swelling. The main goal is to see if the drug is safe and well-tolerated in children, and to measure how it works in their bodies. Researchers will also track how many HAE attacks the children have while on the treatment.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Ionis Investigative Site

    RECRUITING

    Santa Monica, California, 90404, United States

  • Ionis Investigative Site

    RECRUITING

    St Louis, Missouri, 63141, United States

  • Ionis Investigative Site

    RECRUITING

    Cincinnati, Ohio, 45236, United States

Conditions

Explore the condition pages connected to this study.