New drug aims to restore muscle protein in boys with devastating disease

NCT ID NCT04906460

Summary

This study is testing an investigational drug called WVE-N531 for boys with Duchenne muscular dystrophy (DMD) who have a specific genetic mutation. The main goal is to see if the drug is safe and if it can increase levels of a crucial muscle protein called dystrophin. Researchers will also check if the treatment helps improve muscle strength and movement.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Arkansas Children's Hospital

    RECRUITING

    Little Rock, Arkansas, 72202-3500, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Istiklal Hospital/ Clinical Research Unit

    RECRUITING

    Amman, Jordan

    Contact Email: •••••@•••••

    Contact

  • Oxford Children's Hospital, Oxford University Hospitals NHS Foundation Trust

    RECRUITING

    Headington, Oxford, OX3 9DU, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Rare Disease Research LLC

    RECRUITING

    Atlanta, Georgia, 30329, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • The Specialty Hospital (TSH)/ Advanced Clinical Center

    RECRUITING

    Amman, Jordan

    Contact Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.