Breakthrough triple therapy shows promise for Long-Term CF management
NCT ID NCT03525574
Summary
This study followed 507 people with cystic fibrosis to check the long-term safety and effectiveness of a three-drug combination therapy. It focused on patients with a specific genetic mutation (F508del) that causes most CF cases. Researchers monitored lung function, weight, quality of life, and side effects over an extended period to see if benefits were maintained.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Academic Medical Center
Amsterdam, Netherlands
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Akron Children's Hospital
Akron, Ohio, 44308, United States
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Ann & Robert Lurie Children's Hospital of Chicago
Chicago, Illinois, 60611, United States
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Augusta University
Augusta, Georgia, 30912, United States
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Azienda Ospedaliera Universitaria Policlinico G. Martino
Messina, Italy
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Azienda Ospedaliera di Verona-Ospedale Civile Maggiore
Verona, Italy
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Azienda Ospedaliero Universitaria Ospedale Pediatrico Meyer
Florence, Italy
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Azienda Ospedaliero Universitaria Ospendali Riuniti
Ancona, Italy
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Banner University of Arizona Medical Center
Tucson, Arizona, 85724, United States
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Belfast City Hospital
Belfast, United Kingdom
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Billings Clinic Hospital
Billings, Montana, 59101, United States
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British Columbia's Children's Hospital
Vancouver, Canada
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CHU Marseille - Hopital Nord
Marseille, France
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CHU de Nice - Hopital Pasteur
Nice, France
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CHU de Rouen - Hopital Charles Nicolle
Rouen, France
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CTSI Adult Translational Research Unit/Medical College of Wisconsin/Froedtert Hospital
Milwaukee, Wisconsin, 53226, United States
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Central Florida Pulmonary Group, PA
Orlando, Florida, 32803, United States
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Centre Hospitalier De L'Universite Laval
Québec, Canada
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Centre Hospitalier Lyon Sud
Benite Cedex, France
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Centro Regionale Fibrosi Cistica, A.O. Ospedale San Carlo
Potenza, Italy
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Children's Hospital Los Angeles
Los Angeles, California, 90027, United States
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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Children's Hospital of Richmond at VCU, Children's Pavilion
Richmond, Virginia, 23298, United States
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Children's Hospital of the King's Daughters
Norfolk, Virginia, 23507, United States
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Children's Respiratory and Critical Care Specialists, P.A., Children's Hospitals and Clinics of Minnesota
Minneapolis, Minnesota, 55404, United States
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Children's Specialty Services at North Druid Hills
Atlanta, Georgia, 30324, United States
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Cliniques Universitaires de Bruxelles Hopital Erasme
Brussels, Belgium
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Cystic Fibrosis Center, Children's Hospital of Illinois at OSF Saint Francis Medical Center
Peoria, Illinois, 61637, United States
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Dayton Children's Hospital
Dayton, Ohio, 45404, United States
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Dell Children's Medical Center of Central Texas
Austin, Texas, 78723, United States
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Dr. von Haunersches Kinderspital
München, Germany
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Erasmus Medical Center
Rotterdam, Netherlands
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Fakultni Nemocnice Brno
Brno, Czechia
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Fakultni nemocnice v Motole
Prague, Czechia
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Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
Milan, Italy
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Friedrich-Alexander University of Erlangen-Nuremberg, University Children's Hospital
Erlangen, Germany
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General Hospital of Attika "Sismanoglio"(Adult CF center, NHS)
Marousi, Greece
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Groupe Hospitaler Pellegrin, CHU De Bordeaux
Bordeaux, France
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HagaZiekenhuis van den Haag
The Hague, Netherlands
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Hannover Medical School
Hanover, Germany
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Harper University Hospital
Detroit, Michigan, 48201, United States
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Heart of England NHS Foundation Trust, Birmingham Heartlands Hospital
Birmingham, United Kingdom
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Hopital Cochin
Paris, France
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Hopital Foch (Suresnes), Hopital Foch, Adultes
Suresnes, France
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IRCCS Istituto Giannina Gaslini-Ospedale Pediatrico
Genova, Italy
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Joe DiMaggio Cystic Fibrosis & Pulmonary Center
Hollywood, Florida, 33021, United States
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Johannes Gutenberg-Universitaet
Mainz, Germany
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Justus-Leibig-Universitat Zentrum fur Kinderheilkunde und Jugendmedizin
Giessen, Germany
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Kaiser Permanente
Oakland, California, 94611, United States
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Karolinska Universitetssjukhuset, Huddinge
Stockholm, Sweden
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King's College Hospital
London, United Kingdom
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LKH - Universitätsklinikum der PMU Salzburg
Salzburg, Austria
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Leeds General Infirmary
Leeds, United Kingdom
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Maine Medical Partners
Portland, Maine, 04102, United States
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Massachusetts General Hospital Cystic Fibrosis Center Clinical Research Center
Boston, Massachusetts, 02114, United States
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Mater Misericordiae Ltd
South Brisbane, Australia
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McGill University Health Centre, Glen Site, Montreal Children's Hospital
Montreal, Canada
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Medical University of South Carolina
Charleston, South Carolina, 29425, United States
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Medizinische Universitat Wien
Vienna, Austria
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Medizinische Universität Innsbruck
Innsbruck, Austria
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Miller Children's Hospital / Long Beach Memorial
Long Beach, California, 90806, United States
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Morristown Medical Center
Morristown, New Jersey, 07960, United States
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National Jewish Health
Denver, Colorado, 80206, United States
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
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Nebraska Medical Center
Omaha, Nebraska, 68198, United States
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Nemours Children's Hospital
Orlando, Florida, 32827, United States
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Nemours Children's Specialty Care
Jacksonville, Florida, 32207, United States
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New York Medical College
Valhalla, New York, 10595, United States
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Northwestern Memorial Hospital
Chicago, Illinois, 60611, United States
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ProMedica Toledo Hospital/Toledo Children's Hospital/Pediatric Pulmonary & Cystic Fibrosis Center
Toledo, Ohio, 43606, United States
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Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center
Cleveland, Ohio, 44106, United States
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Royal Devon and Exeter NHS Foundation Trust, Royal Devon and Exeter Hospital
Exeter, United Kingdom
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Royal Manchester Children's Hospital
Manchester, United Kingdom
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Southampton General Hospital
Southampton, United Kingdom
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St. Paul's Hospital
Vancouver, Canada
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Tampa General Hospital Cardiac and Lung Transplant Clinic
Tampa, Florida, 33606, United States
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The Children's Hospital at Westmead
Westmead, Australia
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The Cystic Fibrosis Center, Mount Sinai Beth Israel
New York, New York, 10003, United States
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The Hospital for Sick Children
Toronto, Canada
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The Royal Children's Hospital
Parkville, Australia
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The University of Kansas Medical Center
Kansas City, Kansas, 66160, United States
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The University of Texas Southwestern Medical Center
Dallas, Texas, 75390, United States
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Tulane Medical Center
New Orleans, Louisiana, 70112, United States
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UC Health Holmes
Cincinnati, Ohio, 45220, United States
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UCSF Gateway Medical Center
San Francisco, California, 94143, United States
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UMC St. Radboud
Nijmegen, Netherlands
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UNC Marsico Clinical Research Center
Chapel Hill, North Carolina, 27517, United States
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UNM Clinical and Translational Science Center
Albuquerque, New Mexico, 87131, United States
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UZ Antwerpen
Edegem, Belgium
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Universitaetsklinikum Tuebingen Klinik fuer Kinder- und Jugendmedizin
Tübingen, Germany
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Universitair Ziekenhuis Brussel - Campus Jette
Brussels, Belgium
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Universitair Ziekenhuis Gent
Ghent, Belgium
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Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg
Leuven, Belgium
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University Hospital Wuerzburg
Würzburg, Germany
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University Medical Center, Utrecht, Department of Pulmonology and Tuberculosis
Heidelberglaan, Netherlands
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University of Arkansas for Medical Sciences
Little Rock, Arkansas, 72205, United States
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University of Calgary Medical Clinic of the Foothills Medical Centre
Calgary, Canada
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University of California Davis Medical Center
Sacramento, California, 95817, United States
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University of Florida, Shands Hospital
Gainesville, Florida, 32610, United States
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University of Graz
Graz, Austria
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University of Oklahoma Health Sciences Center
Oklahoma City, Oklahoma, 73104, United States
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University of Virginia Primary Care Center
Charlottesville, Virginia, 22908, United States
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University of Washington Medical Center
Seattle, Washington, 98195, United States
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University of Wisconsin Hospitals and Clinics
Madison, Wisconsin, 53792, United States
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Valley Children's Hospital
Madera, California, 93636, United States
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Vermont Lung Center
Colchester, Vermont, 05446, United States
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West Virginia University
Morgantown, West Virginia, 26506, United States
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Western General Hospital
Edinburgh, United Kingdom
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Westmead Hospital
Westmead, Australia
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Women & Children's Hospital
North Adelaide, Australia
Conditions
Explore the condition pages connected to this study.