New drug shows promise for rare overgrowth conditions

NCT ID NCT06975618

First seen Jun 25, 2026 · Last updated Jun 30, 2026 · Updated 3 times

Summary

This study tests a new drug called CYH33 in people with rare conditions that cause abnormal tissue growth and blood vessel malformations (PROS and PRVM). The trial has two phases: phase I finds the safest dose, and phase II checks if the drug shrinks growths. About 141 adults and adolescents will take part.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

CYH33 (a PI3Kα inhibitor)

What this could lead to

If successful, this could lead to a new treatment option that shrinks abnormal growths and improves symptoms for people with PROS and PRVM.

What could go wrong

This is an early-phase trial (phase I/II) with a small number of participants, so safety and effectiveness are not yet proven. The drug may cause side effects or fail to show benefit.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

PIK3CA-related overgrowth spectrum

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Capital Center for Children's Health, Capital Medical University

    RECRUITING

    Beijing, Beijing Municipality, 100000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Fujian Medical University Union Hospital

    RECRUITING

    Fuzhou, Fujian, 350001, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Gifu University Hospital

    RECRUITING

    Gifu, 501-1194, Japan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Guangzhou Women and Children's Medical Center

    NOT_YET_RECRUITING

    Guangzhou, Guangdong, 510000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Henan Provincial People's Hospital

    RECRUITING

    Zhengzhou, Henan, 450003, China

    Contact

    Contact

  • Kyorin University Hospital

    RECRUITING

    Mitaka, Tokyo, 181-8611, Japan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • National Hospital Organization Kobe Medical Center

    RECRUITING

    Kobe, Hyōgo, 654-0155, Japan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Plastic Surgery Hospital, Chinese Academy of Medical Sciences

    RECRUITING

    Beijing, Beijing Municipality, 100144, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Shanghai Ninth People Hospital, Shanghai Jiaotong University School of Medicine

    RECRUITING

    Shanghai, Shanghai Municipality, 200011, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Shinshu University Hospital

    RECRUITING

    Matsumoto, Nagano, 390-8621, Japan

    Contact

    Contact

  • The Second Xiangya Hospital of Central South University

    RECRUITING

    Changsha, Hunan, 410011, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

    Contact

  • Tohoku University Hospital

    RECRUITING

    Sendai, Miyagi, 980-8574, Japan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Tonan Hospital

    RECRUITING

    Sapporo, Hokkaido, 060-0004, Japan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • West China Hospital of Sichuan University

    RECRUITING

    Chengdu, Sichuan, 610041, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Yokohama City University Hospital

    RECRUITING

    Yokohama, Kanagawa, 236-0004, Japan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact