Gene editing offers hope for blood disorder patients
NCT ID NCT06328764
First seen Feb 10, 2026 · Last updated May 14, 2026 · Updated 15 times
Summary
This early-stage study tests a new gene-edited stem cell treatment (CS-101) for people with beta-thalassemia, a severe blood disorder requiring frequent transfusions. Ten participants aged 6 to 35 will receive their own genetically modified stem cells to see if it can safely reduce or eliminate the need for blood transfusions. The main goals are checking safety and whether patients can go without transfusions for at least six months.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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The First Affiliated Hospital of Guangxi Medical University
Nanning, Guangxi, China
Conditions
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