Lifeline offered to haemophilia patients exhausting all options

NCT ID NCT04921956

Summary

This program provides free, daily injections of the experimental drug concizumab to people with congenital haemophilia who cannot be adequately treated with currently approved medicines. It is designed for patients who have developed inhibitors to standard treatments or have poor vein access, making regular infusions difficult. Participants will receive the drug and be closely monitored for safety and effectiveness for several years, with regular clinic visits and blood tests.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Augusta University

    AVAILABLE

    Augusta, Georgia, 30912, United States

  • BI-LO Chrt Childn's Cancer Ctr

    AVAILABLE

    Greenville, South Carolina, 29605, United States

  • Children's Hosp-New Orleans

    AVAILABLE

    New Orleans, Louisiana, 70118, United States

  • Children's Hospital Los Angeles - Endocrinology

    AVAILABLE

    Los Angeles, California, 90027, United States

  • Children's Hospital of Michigan

    AVAILABLE

    Detroit, Michigan, 48201, United States

  • Children's Nebraska

    AVAILABLE

    Omaha, Nebraska, 68114, United States

  • Childrens Hospital of Chicago

    AVAILABLE

    Chicago, Illinois, 60611, United States

  • Connecticut Children's Medical Center

    AVAILABLE

    Hartford, Connecticut, 06106, United States

  • Cook Children's Hospital-Hematology-Oncology

    AVAILABLE

    Fort Worth, Texas, 76104, United States

  • ECU Sickle Cell Comp Clinic

    AVAILABLE

    Greenville, North Carolina, 27834, United States

  • Georgetown University Medical Center

    AVAILABLE

    Washington D.C., District of Columbia, 20007, United States

  • Indiana Hemophilia-Thromb Ctr

    AVAILABLE

    Indianapolis, Indiana, 46260, United States

  • Koagulationsmottagningen

    AVAILABLE

    Solna, 171 64, Sweden

  • Louisiana Ctr for Adv Med-LCAM

    AVAILABLE

    Madison, Mississippi, 39110, United States

  • Memorial Health University Medical Center

    AVAILABLE

    Savannah, Georgia, 31404, United States

  • Nationwide Children's Hospital

    AVAILABLE

    Columbus, Ohio, 43205, United States

  • Penn State Hershey Medical Center

    AVAILABLE

    Hershey, Pennsylvania, 17033, United States

  • Southern Specialty Clinic

    AVAILABLE

    Flowood, Mississippi, 39232, United States

  • St. Luke's Mountain States Tumor Institute

    AVAILABLE

    Boise, Idaho, 83712, United States

  • Texas Children's Hospital_Houston

    AVAILABLE

    Houston, Texas, 77030, United States

  • The Children's Mercy Hospital

    AVAILABLE

    Kansas City, Missouri, 64108, United States

  • UMHAT Sveti Georgi EAD, Plovdiv, Clinic of Pediatrics

    AVAILABLE

    Plovdiv, 4002, Bulgaria

  • Univ TX Hlth Sci Ctr Houston

    AVAILABLE

    Houston, Texas, 77030, United States

  • University of California San Francisco UCSF

    AVAILABLE

    San Francisco, California, 94158, United States

  • Virginia Commonwealth University_Richmond_1

    AVAILABLE

    Richmond, Virginia, 23298-0461, United States

Conditions

Explore the condition pages connected to this study.