New cell therapy aims to reduce chemo side effects for rare blood disease
NCT ID NCT04784052
First seen Jan 30, 2026 · Last updated May 22, 2026 · Updated 12 times
Summary
This study tests a new way to do stem cell transplants for people with Fanconi Anemia, a rare genetic condition that causes bone marrow failure. Instead of strong chemotherapy, patients get a milder prep treatment that includes an experimental antibody called JSP191. The goal is to safely replace damaged blood cells with healthy donor cells and reduce serious side effects. About 18 participants will be followed for up to 2 years after the transplant.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Stanford University
RECRUITINGStanford, California, 94305, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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