Could cannabis compound calm symptoms of devastating childhood disease?

NCT ID NCT06333041

Summary

This study aims to see if a purified form of cannabidiol (CBD), a compound from the cannabis plant, can safely help manage the difficult behavioral symptoms and improve daily functioning in children with Sanfilippo syndrome, a rare and severe genetic disorder. About 35 participants will take either the CBD medication or a placebo for periods of time, and caregivers will report on changes in behavior, mood, and sleep. The goal is to find a new way to ease symptoms for which there are currently no approved treatments.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • The Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center

    Torrance, California, 90502, United States

    Contact Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.